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maple syrup urine disease: Facts & Related Content
News •
Study demonstrates successful gene therapy for maple syrup urine disease
• Feb. 28, 2025, 10:38 PM ET (News-Medical)
Gene therapy developed for maple syrup urine disease shows promise
• Feb. 28, 2025, 5:23 AM ET (Medical Xpress)
Facts
Also Known As | MSUD |
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inborn error of metabolismphenylketonuriacystinosisalbinismalkaptonuriacystinuriacystathioninuriaHartnup diseasehomocystinuriatyrosinemiade Toni–Fanconi syndrome
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